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Clinical trial

A Real-World Study of Clinical Use of Available Treatments for Pediatric Patients With Spinal Muscular Atrophy

Novartis PharmaceuticalsCompletedStarted Nov 22, 2011213 enrolledCzechiaNCT07474311

Abstract

The aim of this study was to evaluate real-world treatment patterns and clinical outcomes in pediatric SMA patients in the Czech and Slovak Republics, using data from the Registry of muscular Dystrophy (REaDY).

Keywords

Spinal Muscular AtrophyReal-World EvidenceRetrospective StudyPatient RegistryDisease-Modifying TherapyMuscular Atrophy, Spinal

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